BioMarin Drug Speeds Growth in Children With Dwarfism for Years

Children with the most common form of dwarfism grew at almost the same pace as their average-sized peers after getting daily injections of an experimental medicine from BioMarin Pharmaceutical Inc., and the faster rate lasted for three-and-a-half years.

The research published June 18 in the New England Journal of Medicine showed an intermediate dose of vosoritide increased growth in children with achondroplasia by about half an inch per year, giving them almost 2.2 inches of gain in height each year, similar to unaffected kids their age. While a lower dose led to fewer gains, a higher amount didn’t increase the ...